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@moatrx
• 2 weeks ago
Posted a new blog:
GCC FABRY DISEASE LAUNCH READINESS
GCC FABRY DISEASE LAUNCH READINESS
Both approved Fabry ERTs are already NPHC-covered in the GCC, so the opening is the 30 to 50 patient ADA-positive cohort no one serves.
Unusually for GCC rare...
