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@moatrx
• one week ago
Posted a new blog:
GCC SICKLE CELL DISEASE LAUNCH READINESS
GCC SICKLE CELL DISEASE LAUNCH READINESS
GCC sickle cell disease affects 200,000 to 250,000 patients, yet zero novel SFDA-registered therapy exists since crizanlizumab's 2023 withdrawal.
Hydroxyurea is...



