@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
GCC FABRY DISEASE DISEASE LANDSCAPE
GCC FABRY DISEASE DISEASE LANDSCAPE
GCC Fabry disease access is infrastructure-gated, not formulary-gated: both ERT and oral therapy are covered, yet diagnosis in women lags.
Fabry disease prevalence...
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
US DRAVET SYNDROME DISEASE LANDSCAPE
US DRAVET SYNDROME DISEASE LANDSCAPE
Dravet syndrome hits 1 in 15,700 US births and carries one of epilepsy's highest documented SUDEP rates.
Dravet syndrome is a severe developmental and epileptic...
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
UK DRAVET SYNDROME DISEASE LANDSCAPE
UK DRAVET SYNDROME DISEASE LANDSCAPE
Free NHS SCN1A testing confirms 75% of UK Dravet diagnoses, feeding a NICE-sequenced cannabidiol-then-fenfluramine treatment algorithm.
Dravet syndrome is a...
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
US COPD DISEASE LANDSCAPE
US COPD DISEASE LANDSCAPE
Roughly 14 million US adults are diagnosed with COPD, but the blood eosinophil count now decides who reaches a biologic.
COPD remains one of the largest...
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
US COLD AGGLUTININ DISEASE DISEASE LANDSCAPE
US COLD AGGLUTININ DISEASE DISEASE LANDSCAPE
Cold agglutinin disease affects an estimated 5,000 Americans, and separating primary CAD from secondary cold agglutinin syndrome decides who is even eligible for...
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
US HR+/HER2- BREAST CANCER DISEASE LANDSCAPE
US HR+/HER2- BREAST CANCER DISEASE LANDSCAPE
HR+/HER2- breast cancer is 68% of US cases, but the 20-30% who recur to metastatic disease define the market.
Breast cancer is the most common non-skin cancer in...
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
US ATTR AMYLOIDOSIS DISEASE LANDSCAPE
US ATTR AMYLOIDOSIS DISEASE LANDSCAPE
An estimated 100,000 to 150,000 Americans have ATTR cardiomyopathy, yet most remain undiagnosed despite a scan that can confirm it without biopsy....
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
UK ATTR AMYLOIDOSIS DISEASE LANDSCAPE
UK ATTR AMYLOIDOSIS DISEASE LANDSCAPE
NHS Tc-PYP scintigraphy lifted UK ATTR-CM diagnoses to 2,000-5,000 a year, up from fewer than 500 before the pathway existed in 2021.
Transthyretin (ATTR)...
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
GCC ATTR AMYLOIDOSIS DISEASE LANDSCAPE
GCC ATTR AMYLOIDOSIS DISEASE LANDSCAPE
Fewer than 1,000 of an estimated 15,000-25,000 GCC ATTR-CM patients are diagnosed, under 5%, largely from missing Tc-PYP scans.
Transthyretin amyloidosis causes...
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
US ATOPIC DERMATITIS DISEASE LANDSCAPE
US ATOPIC DERMATITIS DISEASE LANDSCAPE
16.5 million US adults live with atopic dermatitis, yet only the roughly 40% with moderate-to-severe disease enter the biologic-eligible commercial segment.
Atopic...
@moatrx
• 2 weeks ago
• comments: 0
Posted a new blog:
US ALZHEIMER'S DISEASE DISEASE LANDSCAPE
US ALZHEIMER'S DISEASE DISEASE LANDSCAPE
7.2 million Americans have Alzheimer's dementia, but anti-amyloid therapy reaches only the amyloid-confirmed MCI and mild-dementia window, not the whole population....
